About the organization
Mission : To develop treatments for neuromuscular and neuro-ophthalmological diseases that currently lack treatment options, such as Leber's hereditary optic neuropathy (LHON), Duchenne muscular dystrophy (DMD), congenital muscular dystrophy (CMD) and primary progressive multiple sclerosis (PPMS).
Vision : We are passionate about improving patients’ quality of life and are well on the way to becoming leaders in rare mitochondrial and neuromuscular disorders.
Organization primary focus : Neuromuscular and neuro-ophthalmological rare diseases
Contact us for
General partnerships, Good practice sharing, Opportunities for patient engagement collaborations, Speaking opportunities, Participation in task forces and related initiatives, publications related to patient centricity and engagement within industry
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